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CRISPRi
MBNL
Myopathies
Transcriptomics
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Dermatomyositis
Errance diagnostique
OPMD
Genotype phenotype correlation
Cell therapy
Calcium
Trinucleotide repeat expansion
Lamin A/C LMNA gene
Myositis
Skeletal muscle
Treatment
PABPN1
Nuclear envelope
Rare diseases
Myotonic dystrophy
Transgenic mouse model
Muscle regeneration
Mouse model
Inflammation
Heart failure
Therapy
Mechanotransduction
Actin
Laminopathies
Aged
Cytoskeleton
Outcome measures
Neuromuscular disease
Heart
Animals
Aging
Clinical trials
RNA interference
Autoimmune diseases
Motoneuron
Myotonic dystrophy type 1
Autophagy
LMNA
Neuromuscular diseases
CTG repeat contractions
Congenital myopathy
Antisense oligonucleotides
AAV
Long read sequencing
Myotonic Dystrophy
Fabry disease
Centronuclear myopathy
CMS
Satellite cells
Humans
Muscular dystrophy
Autoantibodies
Alternative splicing
COVID-19
Dynamin 2
Myasthenia gravis
Exercise
Lamin A/C
FSHD
Diagnosis
Myasthenia Gravis MG
DMD
Fibrosis
Autoimmunity
Amyotrophic lateral sclerosis
Muscle
Dystrophin
Biomarkers
Cardiomyopathy
LMNA gene
Myotonic Dystrophy type 1
Satellite cell
Regeneration
Rare neuromuscular diseases
Laminopathy
Male
Congenital muscular dystrophy
Neuromuscular junction
RNA biology
Cancer
Brain
Myoblasts
Thérapie génique
Astrocyte
Laminopathie
ALS
Myopathy
Dilated cardiomyopathy
Becker muscular dystrophy
Myogenesis
Gene therapy
Glutamate
Thymus
Duchenne muscular dystrophy